News

July 17, 2020July 17, 2020

Stem Cell-Based Therapy Successfully Treats Severe Neurotrophic Keratitis, Study Shows

News

A stem cell-based graft therapy using patients’ tissue successfully treated people with severe neurotrophic keratitis, significantly correcting cornea damage and vision in all cases, a pilot study demonstrated. The study, ... Read more

July 10, 2020July 10, 2020

National Survey Seeks to Assess Full Social, Economic Burdens of Rare Diseases in US

News, syndicated

The EveryLife Foundation for Rare Diseases has launched a nationwide National Burden of Rare Disease Survey to measure the full implications, economic and social, of living with rare disease in ... Read more

June 26, 2020June 26, 2020

Oxervate Eyedrops Improve Corneal Sensitivity in NK, Trials Show

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Oxervate (cenegermin) eyedrops improved corneal sensitivity in people with neurotrophic keratitis (NK), according to the results of two Phase 2 trials. Those results had been expected to be presented at the ... Read more

June 24, 2020July 24, 2020

Case Study: Herpes Zoster Ophthalmicus May Lead to Early, Severe Keratouveitis

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Two patients with herpes zoster ophthalmicus (HZO) developed an early and severe inflammation of both the cornea and the uveal tract — the pigmented inside lining of the eye — ... Read more

June 22, 2020July 28, 2020

Alexion Charitable Foundation Giving $1.1M to Assist Rare Disease Community During Pandemic

News, syndicated

The Alexion Charitable Foundation has awarded $1.1 million in grants to programs that support those with rare diseases during the COVID-19 pandemic, the organization recently announced. The grants will support ... Read more

June 12, 2020June 12, 2020

Study: Self-retained, Cryopreserved Amniotic Membranes May Heal Corneal Ulcers

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Self-retained, cryopreserved amniotic membranes (cAM) show promise in treating corneal ulcers, especially those resulting from underlying neurotrophic keratitis (NK), according to a recent study. In a retrospective review, researchers found ... Read more

June 10, 2020June 10, 2020

Coalition Will Address Racial Disparities in Rare Disease Communities

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The Black Women’s Health Imperative (BWHI) recently created a Rare Disease Diversity Coalition focused on reducing racial disparities in the rare disease community. Getting a timely and accurate diagnosis for a disease ... Read more

June 5, 2020June 5, 2020

New Questionnaire Aims to Capture Patients’ View of Neurotrophic Keratitis

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A questionnaire that assesses patient-reported symptoms and the impact of these symptoms on daily life activities is being developed specifically for people with neurotrophic keratitis (NK), a study reports. Reviewed ... Read more

May 29, 2020May 29, 2020

Off-label Use of EGF Ointment Seen to Quickly Promote Corneal Healing

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An ointment containing epidermal growth factor (EGF) — a small protein that stimulates the growth of cells making up the surface of different tissues — can promote tissue healing, improve ... Read more

May 29, 2020May 29, 2020

COVID-19 Delaying Rare Disease and Gene Therapy Trials, Pharma Execs Say

News, syndicated

While the ongoing COVID-19 pandemic won’t have much of an impact on cash available for new biotech startups, it has begun to cause delays in the development of gene therapies ... Read more